First-in-human mutation-targeted siRNA phase Ib trial of an inherited skin disorder.
Leachman SA, Hickerson RP, Schwartz ME, Bullough EE, Hutcherson SL, Boucher KM, Hansen CD, Eliason MJ, Srivatsa GS, Kornbrust DJ, Smith FJ, McLean WI, Milstone LM, Kaspar RL.
Leachman SA, et al. Among authors: srivatsa gs.
Mol Ther. 2010 Feb;18(2):442-6. doi: 10.1038/mt.2009.273. Epub 2009 Nov 24.
Mol Ther. 2010.
PMID: 19935778
Free PMC article.
Clinical Trial.