Optimizing ADAMTS13 prophylaxis to reduce relapse and organ failure in congenital thrombotic thrombocytopenic purpura.
Joly BS, Joseph A, Bouzid R, Boisseau P, Kwon T, Dossier C, Gouge-Biebuyck N, Boyer O, Tsatsaris V, Harambat J, Delmas Y, Moranne O, Sellier-Leclerc AL, Marie M, Barbet C, Provôt F, Benhamou Y, Veyradier A, Coppo P, Augusto JF, Azoulay E, Barbay V, Benhamou Y, Arnaud J, Charvet-Rumpler A, Chauveau D, Choukroun G, Coindre JP, Coppo P, Delmas Y, Celia S, Dossier A, Simon V, Frémeaux-Bacchi V, Galicier L, Grangé S, Guidet B, Halimi JM, Antoine N, Jacobs F, Joly B, Kanouni T, Kaplanski G, Virginie R, Le Guern V, Moulin B, Rebibou JM, Ojeda Uribe M, Parquet N, Pène F, Perez P, Poullin P, Pouteil-Noble C, Presne C, Provôt F, Laurent M, Saheb S, Seguin A, Servais A, Stépanian A, Veyradier A, Vigneau C, Wynckel A, Zunic P, Krummel T, Ulrich M, Hertig A, Benoît S, Laurent G, Le Quintrec M, Kwon T, Chatelet V, Ducheyron D, Martis N, Marie M, Ribes D, Ronchetti AM.
Joly BS, et al. Among authors: kanouni t.
Blood Adv. 2026 Mar 10;10(5):1831-1842. doi: 10.1182/bloodadvances.2025017638.
Blood Adv. 2026.
PMID: 40875883
Free PMC article.