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Year Number of Results
2003 4
2004 2
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2006 1
2007 5
2008 6
2009 13
2010 6
2011 7
2012 3
2013 4
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2015 5
2016 4
2017 8
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112 results

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Page 1
ELP1 Gene Augmentation Restores Visual Function in a Mouse Model of Familial Dysautonomia.
Cheng HC, Koli S, Lewis K, Anvarinia Y, Liu Y, Erdoes M, Keiper CE, Estelien R, Chagnon M, Vandenberghe LH, Gao D, Lefcort F, Morini E, Slaugenhaupt SA, Chekuri A. Cheng HC, et al. Among authors: vandenberghe lh. bioRxiv [Preprint]. 2026 Jan 11:2026.01.09.698339. doi: 10.64898/2026.01.09.698339. bioRxiv. 2026. PMID: 41542655 Free PMC article. Preprint.
AAV2-mediated intravitreal delivery of exon-specific U1 snRNA rescues optic neuropathy in familial dysautonomia.
Chekuri A, Kondabolu K, Kirchner EG, Koli S, Chagnon M, Krasniqi-Vanmeter D, Stern ME, Bolduc J, Romano G, Pagani F, Vandenberghe LH, Morini E, Slaugenhaupt SA. Chekuri A, et al. Among authors: vandenberghe lh. Mol Ther Nucleic Acids. 2025 Dec 9;37(1):102788. doi: 10.1016/j.omtn.2025.102788. eCollection 2026 Mar 12. Mol Ther Nucleic Acids. 2025. PMID: 41536810 Free PMC article.
AAV2-mediated intravitreal delivery of exon-specific U1 snRNA rescues optic neuropathy in a mouse model of familial dysautonomia.
Chekuri A, Kondabolu K, Kirchner EG, Koli S, Chagnon M, Krasniqi-Vanmeter D, Stern ME, Bolduc J, Romano G, Pagani F, Vandenberghe LH, Morini E, Slaugenhaupt SA. Chekuri A, et al. Among authors: vandenberghe lh. bioRxiv [Preprint]. 2025 Aug 21:2025.08.21.671454. doi: 10.1101/2025.08.21.671454. bioRxiv. 2025. Update in: Mol Ther Nucleic Acids. 2025 Dec 09;37(1):102788. doi: 10.1016/j.omtn.2025.102788. PMID: 40894547 Free PMC article. Updated. Preprint.
Boost and Increased Antibody Breadth Following a Second Dose of PARVAX for SARS-CoV-2 in Mice and Nonhuman Primates.
Bhatt U, Herate C, Estelien R, Relouzat F, Dereuddre-Bosquet N, Maciorowski D, Diop C, Couto E, Staiti J, Cavarelli M, Bossevot L, Sconosciuti Q, Bouchard P, Le Grand R, Vandenberghe LH, Zabaleta N. Bhatt U, et al. Among authors: vandenberghe lh. Vaccines (Basel). 2024 Aug 2;12(8):882. doi: 10.3390/vaccines12080882. Vaccines (Basel). 2024. PMID: 39204008 Free PMC article.
Subretinal gene therapy delays vision loss in a Bardet-Biedl Syndrome type 10 mouse model.
Hsu Y, Bhattarai S, Thompson JM, Mahoney A, Thomas J, Mayer SK, Datta P, Garrison J, Searby CC, Vandenberghe LH, Seo S, Sheffield VC, Drack AV. Hsu Y, et al. Among authors: vandenberghe lh. Mol Ther Nucleic Acids. 2022 Dec 12;31:164-181. doi: 10.1016/j.omtn.2022.12.007. eCollection 2023 Mar 14. Mol Ther Nucleic Acids. 2022. PMID: 36700052 Free PMC article.
Ancestral library identifies conserved reprogrammable liver motif on AAV capsid.
Zinn E, Unzu C, Schmit PF, Turunen HT, Zabaleta N, Sanmiguel J, Fieldsend A, Bhatt U, Diop C, Merkel E, Gurrala R, Peacker B, Rios C, Messemer K, Santos J, Estelien R, Andres-Mateos E, Wagers AJ, Tipper C, Vandenberghe LH. Zinn E, et al. Among authors: vandenberghe lh. Cell Rep Med. 2022 Nov 15;3(11):100803. doi: 10.1016/j.xcrm.2022.100803. Epub 2022 Nov 2. Cell Rep Med. 2022. PMID: 36327973 Free PMC article.
112 results