Expert consensus on the off-label use of drugs for pediatric rare diseases in China (2025 edition).
Mo X, Deng H, Yang J, Li J, Ouyang S, Chen F, Cui Y, Gao X, Jiang H, Li X, Liu L, Liu J, Qiu L, Rong X, Wen Z, Wang J, Zeng P, Zhang W, Zhao X, Zhou J, Chen J, Chen P, Chen W, Chen Z, Fang R, Fan X, Jia Y, Li Z, Li X, Li X, Lin Y, Liu M, Mai H, Miao J, Wang X, Wang Y, Wang J, Wei L, Wu J, Yu S, Zeng L, Zhang B, Zhang H, Zheng Z, Chen X, Xia S, Zhou W, Sun J, Li Y; Rare Disease Expert Committee of Guangdong Pharmaceutical Association.
Mo X, et al. Among authors: jia y.
Transl Pediatr. 2025 Nov 30;14(11):3094-3124. doi: 10.21037/tp-2025-521. Epub 2025 Nov 26.
Transl Pediatr. 2025.
PMID: 41367530
Free PMC article.
Review.