Theragnosis for Duchenne Muscular Dystrophy.
Luce L, Carcione M, Mazzanti C, Buonfiglio PI, Dalamón V, Mesa L, Dubrovsky A, Corderí J, Giliberto F.
Luce L, et al.
Front Pharmacol. 2021 Jun 3;12:648390. doi: 10.3389/fphar.2021.648390. eCollection 2021.
Front Pharmacol. 2021.
PMID: 34149409
Free PMC article.
We observed different relations among the available targets for exon skipping in the analyzed populations, but a more even proportion of nonsense variants (40%). In conclusion, this manuscript describes the theragnosis carried out in Argentinian dystrophinopathy patients. …
We observed different relations among the available targets for exon skipping in the analyzed populations, but a more even proportion of non …