PubMed Clinical Queries
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Results for Clinical Studies: Therapy/Broad
2 of 2 results sorted by: Most RecentSee all results in PubMed (2)
Efficacy confirmation study of aceneuramic acid administration for GNE myopathy in Japan.
Orphanet J Rare Dis. 2023. PMID: 37568154 Free PMC article. Clinical Trial.
Phase II/III Study of Aceneuramic Acid Administration for GNE Myopathy in Japan.
J Neuromuscul Dis. 2023. PMID: 37125562 Free PMC article. Clinical Trial.