PubMed Clinical Queries
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Results for Clinical Studies: Therapy/Broad
5 of 88 results sorted by: Most RecentSee all results in PubMed (88)
Rapamycin Alleviates Protein Aggregates, Reduces Neuroinflammation, and Rescues Demyelination in Globoid Cell Leukodystrophy.
Cells. 2023. PMID: 37048066 Free PMC article.
Hybrid Nanoparticles as a Novel Tool for Regulating Psychosine-Induced Neuroinflammation and Demyelination In Vitro and Ex vivo.
Neurotherapeutics. 2021. PMID: 34480290 Free PMC article.
Substrate reduction therapy for Krabbe disease and metachromatic leukodystrophy using a novel ceramide galactosyltransferase inhibitor.
Sci Rep. 2021. PMID: 34262084 Free PMC article.
Waning efficacy in a long-term AAV-mediated gene therapy study in the murine model of Krabbe disease.
Mol Ther. 2021. PMID: 33508430 Free PMC article.
Enhanced Efficacy and Increased Long-Term Toxicity of CNS-Directed, AAV-Based Combination Therapy for Krabbe Disease.
Mol Ther. 2021. PMID: 33388420 Free PMC article.