PubMed Clinical Queries
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Results for Clinical Studies: Therapy/Broad
5 of 578 results sorted by: Most RecentSee all results in PubMed (578)
Endogenous glucose production in patients with glycogen storage disease type Ia estimated by oral d-[6,6-2H2]-glucose.
J Clin Endocrinol Metab. 2023. PMID: 37690115
Effect of pharmacological heart failure drugs and gene therapy on Danon's cardiomyopathy.
Biochem Pharmacol. 2023. PMID: 37572991
Population Pharmacokinetic Modeling and Determination of Individual Exposure to Avalglucosidase Alfa in Adolescent and Adult Patients With Late-Onset Pompe Disease: Analysis of Pooled Data From Phase I to III Clinical Trials.
Ther Drug Monit. 2023. PMID: 37556417 Free PMC article.
Characteristics of Patients With Late-Onset Pompe Disease in France: Insights From the French Pompe Registry in 2022.
Neurology. 2023. PMID: 37419682
Home-Based Infusion of Alglucosidase Alfa Can Safely be Implemented in Adults with Late-Onset Pompe Disease: Lessons Learned from 18,380 Infusions.
BioDrugs. 2023. PMID: 37326923 Free PMC article.