PubMed Clinical Queries
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Results for Clinical Studies: Therapy/Broad
5 of 10 results sorted by: Most RecentSee all results in PubMed (10)
The first gene therapy for RPE65 biallelic dystrophy with voretigene neparvovec-rzyl in Brazil.
Ophthalmic Genet. 2022. PMID: 35416119
Gene therapy for RPE65-related retinal disease.
Ophthalmic Genet. 2018. PMID: 30335549 Review.
Overexpression of Type 3 Iodothyronine Deiodinase Reduces Cone Death in the Leber Congenital Amaurosis Model Mice.
Adv Exp Med Biol. 2018. PMID: 29721936
The rapidly evolving state of gene therapy.
FASEB J. 2018. PMID: 31282760 Review.
Evaluation of Ocular Gene Therapy in an Italian Patient Affected by Congenital Leber Amaurosis Type 2 Treated in Both Eyes.
Adv Exp Med Biol. 2016. PMID: 26427456