Defects of the mitochondrial respiratory chain complexes in three pediatric cases with hypotonia and cardiac involvement

J Neurol Sci. 1992 Mar;108(1):105-13. doi: 10.1016/0022-510x(92)90195-q.

Abstract

Three children displaying hypotonia, cardiac involvement and defects of the mitochondrial respiratory chain complexes are reported. The first case showed severe neonatal hypotonia, failure to thrive, hepatomegaly, dilation of the right cardiac cavities, profound lactic acidosis and amino aciduria. The boy died at the age of 7 weeks. In the second case hypotonia, severe cardiomyopathy, cyclic neutropenia, lactic acidosis and 3-methylglutaconic aciduria occurred. The boy died at the age of 27 months. The third case presented at the age of 16 months as an acute hypokinetic hypertrophic cardiomyopathy with transient hypotonia and mild lactic acidosis. Spontaneous clinical remission occurred. In all cases muscle biopsy was performed. Morphological studies failed to show ragged-red fibers but there was lipid storage myopathy and decreased cytochrome c oxidase activity. Biochemical studies confirmed the cytochrome c oxidase deficiency in muscle in all cases. It was associated with complex I III deficiency in case 1 and with severe deficits of all respiratory chain complexes in case 2. Post-mortem studies in case 1 indicated that complex IV was reduced in the liver but not in the heart and quantitative analysis of mtDNA revealed a depletion in muscle. Cases 1 and 2 shared some clinical features with fatal infantile myopathy associated with cytochrome c oxidase deficiency, while case 3 displayed a very unusual clinical presentation. The histochemical enzyme reaction of cytochrome c oxidase is useful for the diagnosis of mitochondrial myopathy because ragged-red fibers may be lacking. Finally, biochemical measurement of the different mitochondrial respiratory chain complexes is required because multiple defects are frequent and occasionally related to mtDNA depletion.

Publication types

  • Case Reports
  • Comparative Study
  • Research Support, Non-U.S. Gov't
  • Review

MeSH terms

  • Abnormalities, Multiple
  • Acidosis, Lactic / enzymology
  • Acidosis, Lactic / genetics
  • Cytochrome-c Oxidase Deficiency*
  • DNA, Mitochondrial / genetics*
  • Electron Transport Complex IV / genetics
  • Electron Transport*
  • Heart Failure / enzymology
  • Heart Failure / genetics*
  • Hepatomegaly / enzymology
  • Hepatomegaly / genetics
  • Humans
  • Infant
  • Lipid Metabolism
  • Liver / pathology
  • Male
  • Mitochondria / enzymology*
  • Muscle Hypotonia / enzymology
  • Muscle Hypotonia / genetics*
  • Muscles / pathology
  • Myocardium / pathology
  • Phenotype
  • Syndrome

Substances

  • DNA, Mitochondrial
  • Electron Transport Complex IV