The effect of haematopoietic stem cell transplant on papules with 'pebbly' appearance in Hunter's syndrome

Br J Dermatol. 2004 Jul;151(1):207-11. doi: 10.1111/j.1365-2133.2004.05944.x.

Abstract

Background: Hunter's syndrome is associated with several cutaneous findings. For instance, papules with 'pebbly' appearance are a specific marker for the disease. However, it remains uncertain whether they disappear after haematopoietic stem cell transplant (HSCT).

Objectives: To investigate the papules with 'pebbly' appearance before and after HSCT in infants with Hunter's syndrome, and to clarify the effect of HSCT on papules.

Patients: We observed five Japanese boys with Hunter's syndrome who had received HSCT at 4-11 years of age.

Results: The post-HSCT physical examinations revealed that papules disappeared completely within 35 days after the transplant with progressive reduction of cutaneous tightness in all the patients. Histochemical findings showed that papules contained a large amount of hyaluronic acid in the extracellular materials of the dermis and sulphated acid mucopolysaccharides in dermal fibroblasts before HSCT.

Conclusions: These results suggest that papules with a 'pebbly' appearance fade away through the digestion of a large amount of hyaluronic acid in cutaneous tissues by normal tissue histiocytes or enzymes of donor origin at an early stage after HSCT.

Publication types

  • Case Reports
  • Review

MeSH terms

  • Child
  • Child, Preschool
  • Extracellular Matrix / metabolism
  • Fibroblasts / metabolism
  • Glycosaminoglycans / metabolism
  • Hematopoietic Stem Cell Transplantation*
  • Histocytochemistry
  • Humans
  • Hyaluronic Acid / metabolism
  • Male
  • Microscopy, Electron
  • Mucopolysaccharidosis II / metabolism
  • Mucopolysaccharidosis II / pathology*
  • Mucopolysaccharidosis II / therapy*
  • Skin / metabolism
  • Skin / pathology*

Substances

  • Glycosaminoglycans
  • Hyaluronic Acid