Detection of point mutations and a gross deletion in six Hunter syndrome patients

Genomics. 1992 Jul;13(3):543-50. doi: 10.1016/0888-7543(92)90123-a.

Abstract

We have used screening with the polymerase chain reaction and chemical mismatch detection of amplified cDNA to detect and characterize deletions and point mutations in six Hunter Syndrome patients. A high degree of mutational heterogeneity was observed. The first patient is completely deleted for the gene coding for alpha-L-iduronate sulfate sulfatase, while the second has a point mutation that creates a stop codon. The third patient shows a point mutation that creates a novel splice site that is preferentially utilized and results in partial loss of one exon in the RNA. Patients 4, 5, and 6 have point mutations resulting in single amino acid substitutions. Four of the six single-base changes observed in this study were examples of transitions of the highly mutable dinucleotide CpG to TpG. This study has demonstrated a procedure capable of detecting all types of mutation that affect the function of the IDS protein and should enable direct carrier and prenatal diagnosis for Hunter syndrome families.

Publication types

  • Research Support, Non-U.S. Gov't

MeSH terms

  • Amino Acid Sequence
  • Base Sequence
  • Chromosome Deletion
  • DNA / genetics
  • DNA Mutational Analysis
  • Humans
  • Iduronate Sulfatase / genetics
  • Molecular Sequence Data
  • Mucopolysaccharidosis II / diagnosis
  • Mucopolysaccharidosis II / enzymology
  • Mucopolysaccharidosis II / genetics*
  • Polymerase Chain Reaction

Substances

  • DNA
  • Iduronate Sulfatase