PTC124, nonsense mutations and Duchenne muscular dystrophy

Neuromuscul Disord. 2007 Oct;17(9-10):719-20. doi: 10.1016/j.nmd.2007.07.001.
No abstract available

MeSH terms

  • Animals
  • Codon, Nonsense / antagonists & inhibitors*
  • Humans
  • Mice
  • Mice, Inbred mdx
  • Muscular Dystrophy, Duchenne / drug therapy*
  • Muscular Dystrophy, Duchenne / genetics*
  • Oxadiazoles / therapeutic use*

Substances

  • Codon, Nonsense
  • Oxadiazoles
  • ataluren