A decade of optimizing drug development for rare neuromuscular disorders through TACT

Nat Rev Drug Discov. 2020 Jan;19(1):1-2. doi: 10.1038/d41573-019-00199-1.
No abstract available

Publication types

  • News

MeSH terms

  • Advisory Committees
  • Drug Development / standards*
  • Humans
  • Neuromuscular Diseases / drug therapy*
  • Patient Care Planning / standards*
  • Rare Diseases / drug therapy*
  • United States