Patisiran in hereditary transthyretin-mediated amyloidosis

Lancet Neurol. 2021 Jan;20(1):21-23. doi: 10.1016/S1474-4422(20)30397-5. Epub 2020 Nov 16.
No abstract available

Publication types

  • Comment

MeSH terms

  • Amyloid Neuropathies, Familial* / genetics
  • Humans
  • Polyneuropathies*
  • Prealbumin / genetics
  • RNA, Small Interfering

Substances

  • Prealbumin
  • RNA, Small Interfering
  • patisiran