RNA-targeted drugs for neuromuscular diseases

Science. 2021 Jan 1;371(6524):29-31. doi: 10.1126/science.aba4515.

Alessandra Ferlini^{1

2}, Aurelie Goyenvalle³, Francesco Muntoni^{4

5}

¹ Unit of Medical Genetics, Department of Medical Science, University of Ferrara, Ferrara, Italy.
² Dubowitz Neuromuscular Centre, UCL Great Ormond Street Institute of Child Health, University College London, London, UK.
³ Université Paris-Saclay, UVSQ, Inserm, END-ICAP, Versailles, France.
⁴ Dubowitz Neuromuscular Centre, UCL Great Ormond Street Institute of Child Health, University College London, London, UK. f.muntoni@ucl.ac.uk.
⁵ NIHR Great Ormond Street Hospital Biomedical Research Centre, London, UK.

No abstract available

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