Methodological challenges in measuring meaningful change in individuals with spinal muscular atrophy

Muscle Nerve. 2021 Dec;64(6):639-640. doi: 10.1002/mus.27442. Epub 2021 Nov 5.

Authors

Maryam Oskoui¹, Beth K Potter²

Affiliations

¹ Departments of Pediatrics and Neurology & Neurosurgery, McGill University, Montréal, Québec, Canada.
² School of Epidemiology and Public Health, University of Ottawa, Ottawa, Ontario, Canada.

PMID: 34687231
DOI: 10.1002/mus.27442

No abstract available

Keywords: SMA; epidemiology; motor function; outcome measure; spinal muscular atrophy.

Publication types

Editorial
Research Support, Non-U.S. Gov't
Comment

MeSH terms

Humans
Muscular Atrophy, Spinal* / diagnosis
Spinal Muscular Atrophies of Childhood* / diagnosis