Impacts and Burden of Niemann pick Type-C: a patient and caregiver perspective.
Mengel E, Patterson MC, Chladek M, Guldberg C, Í Dali C, Symonds T, Lloyd-Price L, Mathieson T, Crowe J, Burbridge C.
Mengel E, et al. Among authors: symonds t.
Orphanet J Rare Dis. 2021 Nov 24;16(1):493. doi: 10.1186/s13023-021-02105-8.
Orphanet J Rare Dis. 2021.
PMID: 34819124
Free PMC article.