Allogeneic cellular gene therapy in hemoglobinopathies--evaluation of hematopoietic SCT in sickle cell anemia.
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Bone Marrow Transplant. 2012 Feb;47(2):227-30. doi: 10.1038/bmt.2011.79. Epub 2011 Apr 18.
Bone Marrow Transplant. 2012.
PMID: 21499319
Clinical Trial.