Protease-resistant modified human β-hexosaminidase B ameliorates symptoms in GM2 gangliosidosis model.
Kitakaze K, Mizutani Y, Sugiyama E, Tasaki C, Tsuji D, Maita N, Hirokawa T, Asanuma D, Kamiya M, Sato K, Setou M, Urano Y, Togawa T, Otaka A, Sakuraba H, Itoh K.
Kitakaze K, et al. Among authors: hirokawa t.
J Clin Invest. 2016 May 2;126(5):1691-703. doi: 10.1172/JCI85300. Epub 2016 Mar 28.
J Clin Invest. 2016.
PMID: 27018595
Free PMC article.