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Page 1
ERN GENTURIS tumour surveillance guidelines for individuals with neurofibromatosis type 1.
Carton C, Evans DG, Blanco I, Friedrich RE, Ferner RE, Farschtschi S, Salvador H, Azizi AA, Mautner V, Röhl C, Peltonen S, Stivaros S, Legius E, Oostenbrink R; ERN GENTURIS NF1 Tumour Management Guideline Group. Carton C, et al. Among authors: azizi aa. EClinicalMedicine. 2023 Jan 13;56:101818. doi: 10.1016/j.eclinm.2022.101818. eCollection 2023 Feb. EClinicalMedicine. 2023. PMID: 36684394 Free PMC article. Review.
Effective targeting of PDGFRA-altered high-grade glioma with avapritinib.
Mayr L, Neyazi S, Schwark K, Trissal M, Beck A, Labelle J, Eder SK, Weiler-Wichtl L, Marques JG, de Biagi-Junior CAO, Lo Cascio C, Chapman O, Sridhar S, Kenkre R, Dutta A, Wang S, Wang J, Hack O, Nascimento A, Nguyen CM, Castellani S, Rozowsky JS, Groves A, Panditharatna E, Cruzeiro GAV, Haase RD, Tabatabai K, Madlener S, Wadden J, Adam T, Kong S, Miclea M, Patel T, Bruckner K, Senfter D, Lämmerer A, Supko J, Guntner AS, Palova H, Neradil J, Stepien N, Lötsch-Gojo D, Berger W, Leiss U, Rosenmayr V, Dorfer C, Dieckmann K, Peyrl A, Azizi AA, Baumgartner A, Slaby O, Pokorna P, Clark LM, Cameron A, Nguyen QD, Wakimoto H, Dubois F, Greenwald NF, Bandopadhayay P, Beroukhim R, Ligon K, Kramm C, Bronsema A, Bailey S, Stucklin AG, Mueller S, Skrypek M, Martinez N, Bowers DC, Jones DTW, Jones C, Jäger N, Sterba J, Müllauer L, Haberler C, Kumar-Sinha C, Chinnaiyan A, Mody R, Chavez L, Furtner J, Koschmann C, Gojo J, Filbin MG. Mayr L, et al. Among authors: azizi aa. Cancer Cell. 2025 Apr 14;43(4):740-756.e8. doi: 10.1016/j.ccell.2025.02.018. Epub 2025 Mar 13. Cancer Cell. 2025. PMID: 40086436 Free PMC article.
LOGGIC/FIREFLY-2: a phase 3, randomized trial of tovorafenib vs. chemotherapy in pediatric and young adult patients with newly diagnosed low-grade glioma harboring an activating RAF alteration.
van Tilburg CM, Kilburn LB, Perreault S, Schmidt R, Azizi AA, Cruz-Martínez O, Zápotocký M, Scheinemann K, Meeteren AYNS, Sehested A, Opocher E, Driever PH, Avula S, Ziegler DS, Capper D, Koch A, Sahm F, Qiu J, Tsao LP, Blackman SC, Manley P, Milde T, Witt R, Jones DTW, Hargrave D, Witt O. van Tilburg CM, et al. Among authors: azizi aa. BMC Cancer. 2024 Jan 30;24(1):147. doi: 10.1186/s12885-024-11820-x. BMC Cancer. 2024. PMID: 38291372 Free PMC article. Clinical Trial.
Evolutionary characterization of lung cancer metastasis.
Hessey S, Bunkum A, Huebner A, Haase K, Grigoriadis K, Naceur-Lombardelli C, Liu WK, Harrigan CF, Grieco C, Marinelli D, Ding B, Martínez-Ruiz C, Pawlik P, Hill MS, Lucas O, Richard C, Pich O, Thol K, Karasaki T, Ward S, Athanasopoulou F, Sivakumar M, Veeriah S, Toncheva A, Rowan AJ, Prymas P, Bridger H, Mitchison M, Borg E, Falzon M, Proctor I, Mahadeva U, Green A, Forster MD, Benafif S, Ahmad T, Lee SM, Papadatos-Pastos D, Naidu B, Langman G, Krebs MG, Oliveira P, Blackhall FH, Summers Y, Weaver J, Le Quesne J, Thomas A, Richards C, Fennell DA, Jogai S, Cave J, Roxburgh P, Fraser S, Kirk A, Blyth KG, Russell P, Hiley CT, Hackshaw A; TRACERx Consortium; TRACERx EVO Consortium; PEACE consortium; Moore DA, Zaccaria S, McGranahan N, Swanton C, Jamal-Hanjani M. Hessey S, et al. Nature. 2026 May;653(8115):911-922. doi: 10.1038/s41586-026-10428-4. Epub 2026 Apr 29. Nature. 2026. PMID: 42056508 Free PMC article.
Sustained Survival Benefit in Recurrent Medulloblastoma by a Metronomic Antiangiogenic Regimen: A Nonrandomized Controlled Trial.
Peyrl A, Chocholous M, Sabel M, Lassaletta A, Sterba J, Leblond P, Nysom K, Torsvik I, Chi SN, Perwein T, Jones N, Holm S, Nyman P, Mörse H, Öberg A, Weiler-Wichtl L, Leiss U, Haberler C, Schmook MT, Mayr L, Dieckmann K, Kool M, Gojo J, Azizi AA, André N, Kieran M, Slavc I. Peyrl A, et al. Among authors: azizi aa. JAMA Oncol. 2023 Dec 1;9(12):1688-1695. doi: 10.1001/jamaoncol.2023.4437. JAMA Oncol. 2023. PMID: 37883081 Free PMC article. Clinical Trial.
Resistance, rebound, and recurrence regrowth patterns in pediatric low-grade glioma treated by MAPK inhibition: A modified Delphi approach to build international consensus-based definitions-International Pediatric Low-Grade Glioma Coalition.
O'Hare P, Cooney T, de Blank P, Gutmann DH, Kieran M, Milde T, Fangusaro J, Fisher M, Avula S, Packer R, Fukuoka K, Mankad K, Mueller S, Waanders AJ, Opocher E, Bouffet E, Raabe E, Werle NE, Azizi AA, Robison NJ, Hernáiz Driever P, Russo M, Schouten N, van Tilburg CM, Sehested A, Grill J, Bandopadhayay P, Kilday JP, Witt O, Ashley DM, Ertl-Wagner BB, Tabori U, Hargrave DR. O'Hare P, et al. Among authors: azizi aa. Neuro Oncol. 2024 Aug 5;26(8):1357-1366. doi: 10.1093/neuonc/noae074. Neuro Oncol. 2024. PMID: 38743009 Free PMC article.
Co-targeting CDK4/6 and MEK reverses mesenchymal transition in therapy-refractory BRAF-altered pediatric high-grade glioma.
Mayr L, Mager L, Gabler-Pamer L, Kirchhofer D, Freund J, Schwark K, Lau B, Machreich S, Senfter D, Neumüller M, Lang A, Madlener S, Laemmerer A, Bruckner K, Jaunecker CN, Robl B, Walter R, Schueler J, Peyrl A, Azizi AA, Dorfer C, Roessler K, Spiegl-Kreinecker S, Haberler C, Federico A, Gopisetty A, Schleiermacher G, Pfister SM, Geoerger B, Chesler L, Vassal G, Kool M, Müllauer L, Koschmann C, Berger W, Gojo J, Lötsch D. Mayr L, et al. Among authors: azizi aa. J Exp Clin Cancer Res. 2026 May 16;45(1):154. doi: 10.1186/s13046-026-03725-3. J Exp Clin Cancer Res. 2026. PMID: 42143334 Free PMC article.
Pediatric high-grade gliomas in patients with neurofibromatosis type 1-A collaborative cohort study from the SIOPE HGG/DIPG working group.
Karremann M, Gerdes T, Gielen GH, Kwiecien R, Perwein T, Hoffmann M, Azizi AA, Babor F, Barrios-Bussmann C, Behrens L, Benesch M, Bertero L, Biassoni V, Bison B, Buttarelli FR, Calaminus G, Claviez A, Distelmaier F, Ebinger M, Elayadi M, Ernst J, Eyrich M, Fleischhack G, Friedrich C, Friker LL, Garre ML, Gerber NU, Gojo J, Hargrave D, Häuser S, Hernaiz-Driever P, Holm S, Jakob M, Knirsch S, Kratz C, Krischer JM, Kühnöl C, Kumirova E, Massimino M, Vinci M, Meijer L, Metzler M, Milanaccio C, La Madrid AM, Morana G, Nussbaumer G, Piccolo G, Pollo B, Reifenberger G, Reimann C, Rosenbaum T, Schiavello E, Sterba J, Sturm D, Szychot E, Valentini C, Vallero SG, Velleuer-Carlberg E, van Buiren M, Mastronuzzi A, van Vuurden D, von Bueren AO, Wiese M, Zinke C, Zlocha J, Pietsch T, Kramm CM. Karremann M, et al. Among authors: azizi aa. Neurooncol Pract. 2025 Oct 7;13(1):71-85. doi: 10.1093/nop/npaf104. eCollection 2026 Feb. Neurooncol Pract. 2025. PMID: 41798124 Free article.
85 results