Skip to main page content
U.S. flag

An official website of the United States government

Dot gov

The .gov means it’s official.
Federal government websites often end in .gov or .mil. Before sharing sensitive information, make sure you’re on a federal government site.

Https

The site is secure.
The https:// ensures that you are connecting to the official website and that any information you provide is encrypted and transmitted securely.

Access keys NCBI Homepage MyNCBI Homepage Main Content Main Navigation

Search Page

Filters

My NCBI Filters

Results by year

Table representation of search results timeline featuring number of search results per year.

Year Number of Results
1968 2
1970 1
1971 1
1972 1
1973 2
1974 1
1975 1
1981 1
1983 1
1984 1
1985 1
1986 2
1987 1
1988 2
1989 3
1991 1
1992 3
1993 4
1994 4
1995 3
1996 7
1997 4
1998 8
1999 5
2000 4
2001 7
2002 9
2003 11
2004 12
2005 15
2006 16
2007 28
2008 20
2009 22
2010 16
2011 20
2012 24
2013 20
2014 22
2015 20
2016 23
2017 22
2018 20
2019 18
2020 21
2021 19
2022 19
2023 17
2024 8

Text availability

Article attribute

Article type

Publication date

Search Results

441 results

Results by year

Filters applied: . Clear all
Page 1
Mucopolysaccharidosis type I.
Wraith JE, Jones S. Wraith JE, et al. Pediatr Endocrinol Rev. 2014 Sep;12 Suppl 1:102-6. Pediatr Endocrinol Rev. 2014. PMID: 25345091 Review.
Mucopolysaccharidoses type I gene therapy.
Hurt SC, Dickson PI, Curiel DT. Hurt SC, et al. J Inherit Metab Dis. 2021 Sep;44(5):1088-1098. doi: 10.1002/jimd.12414. Epub 2021 Jul 9. J Inherit Metab Dis. 2021. PMID: 34189746 Free PMC article. Review.
Hematopoietic Stem- and Progenitor-Cell Gene Therapy for Hurler Syndrome.
Gentner B, Tucci F, Galimberti S, Fumagalli F, De Pellegrin M, Silvani P, Camesasca C, Pontesilli S, Darin S, Ciotti F, Sarzana M, Consiglieri G, Filisetti C, Forni G, Passerini L, Tomasoni D, Cesana D, Calabria A, Spinozzi G, Cicalese MP, Calbi V, Migliavacca M, Barzaghi F, Ferrua F, Gallo V, Miglietta S, Zonari E, Cheruku PS, Forni C, Facchini M, Corti A, Gabaldo M, Zancan S, Gasperini S, Rovelli A, Boelens JJ, Jones SA, Wynn R, Baldoli C, Montini E, Gregori S, Ciceri F, Valsecchi MG, la Marca G, Parini R, Naldini L, Aiuti A, Bernardo ME; MPSI Study Group. Gentner B, et al. N Engl J Med. 2021 Nov 18;385(21):1929-1940. doi: 10.1056/NEJMoa2106596. N Engl J Med. 2021. PMID: 34788506 Clinical Trial.
A few challenges in mucopolysaccharidosis type I.
Bay L, Amartino H, Antacle A, Arberas C, Berretta A, Botto H, Cazalas M, Copiz A, De Cunto C, Drelichman G, Espada G, Eiroa H, Fainboim A, Fano V, Guelber N, Maffey A, Parisi C, Pereyra M, Remondino R, Schenone A, Spécola N, Staciuk R, Zuccaro G. Bay L, et al. Arch Argent Pediatr. 2021 Jun;119(3):e193-e201. doi: 10.5546/aap.2021.e193. Arch Argent Pediatr. 2021. PMID: 34033424 Free article. English, Spanish.
Intra-articular nonviral gene therapy in mucopolysaccharidosis I mice.
Bidone J, Schuh RS, Farinon M, Poletto É, Pasqualim G, de Oliveira PG, Fraga M, Xavier RM, Baldo G, Teixeira HF, Matte U. Bidone J, et al. Int J Pharm. 2018 Sep 5;548(1):151-158. doi: 10.1016/j.ijpharm.2018.06.049. Epub 2018 Jun 27. Int J Pharm. 2018. PMID: 29940298
441 results