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Therapeutic siRNAs for dominant genetic skin disorders including pachyonychia congenita.
J Dermatol Sci. 2008 Sep;51(3):151-7. doi: 10.1016/j.jdermsci.2008.04.003. Epub 2008 May 20.
J Dermatol Sci. 2008.
PMID: 18495438
Free PMC article.
Review.
Stability study of unmodified siRNA and relevance to clinical use.
Hickerson RP, Vlassov AV, Wang Q, Leake D, Ilves H, Gonzalez-Gonzalez E, Contag CH, Johnston BH, Kaspar RL.
Hickerson RP, et al.
Oligonucleotides. 2008 Dec;18(4):345-54. doi: 10.1089/oli.2008.0149.
Oligonucleotides. 2008.
PMID: 18844576
Free PMC article.
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