iPSC-Derived Intestinal Organoids from Cystic Fibrosis Patients Acquire CFTR Activity upon TALEN-Mediated Repair of the p.F508del Mutation.
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Mol Ther Methods Clin Dev. 2020 Apr 18;17:858-870. doi: 10.1016/j.omtm.2020.04.005. eCollection 2020 Jun 12.
Mol Ther Methods Clin Dev. 2020.
PMID: 32373648
Free PMC article.